Weekly Spotlight - 27.11.24

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Latest News

Anastrozole Boosts Height in Children with Adrenal Disorder

Anastrozole, a medication typically used for breast cancer, has been found to increase height in children with congenital adrenal hyperplasia (CAH) by reducing androgen levels, which can help manage growth issues associated with the condition. This treatment shows promise in improving the quality of life for these children.

FDA Approves BridgeBio Pharma's Attr-CM Treatment, Atrurby (Acoramidis) for Rare Heart Condition

BridgeBio Pharma has received FDA approval for ATRUBY (acoramidis), a treatment for transthyretin amyloid cardiomyopathy (ATTR-CM). This approval highlights advancements in rare disease treatments from BridgeBio Pharma, which could inspire hope for similar breakthroughs in other conditions which they cover, such as congenital adrenal hyperplasia.